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Yahoo answers: What is gaucher disease in a really easy definition?
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I find lots of good sites about gaucher disease but im not sure what it really is and what the words mean. I need an easy definition to help me understand it more.
08/14/09 -
Gaucher's Disease is a Lysosomal Storage Disease and is an inherited metabolic disorder that results from malfunctions in the cell's lysosome (which breaks down organelles within the cell), caused...
Latest news about gaucher s disease
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Research and Markets: Global Gaucher's Disease Epidemiology and Patient ...
This report provides insights into Gaucher's Disease epidemiology, Gaucher's Disease diagnosed patients, and Gaucher's Disease treatment rate for top seven pharmaceutical markets. The study measures key indicators such as prevalence of Gaucher's
Source: http://www.businesswire.com/news/home/20150122006207/en/Research-Markets-Global-Gauchers-Disease-Epidemiology-Patient -
Sanofis Cerdelga Cleared in the EU for Gaucher Disease
The European Commission (EC) has approved Sanofi's (SNY - Analyst Report) first line oral therapy, Cerdelga, for the treatment of certain adults suffering from Gaucher disease type I. The company said that adults who metabolize Cerdelga more rapidly or
Source: http://www.zacks.com/stock/news/161615/sanofis-cerdelga-cleared-in-the-eu-for-gaucher-disease -
Pricing uncertainty for orphan drugs and innovative new drugs
Cerezyme is an orphan drug which was approved by the European Medicines Agency in 1997 for the treatment of Gaucher's disease. The disease is considered to be an ultra-orphan disease, meaning that it is prevalent in only one case per 50,000 to
Source: http://www.internationallawoffice.com/newsletters/detail.aspx?g%3Dd6898991-48db-4e51-b604-910a69790d69 -
FDA approves new drug to treat a form of Gaucher disease
In one randomized, double-blind, placebo-controlled, multicenter clinical trial the safety and effectiveness of Cerdelga were evaluated in 40 participants with Type 1 Gaucher's disease who had not previously received enzyme replacement therapy
Source: http://www.fda.gov/NewsEvents/Newsroom/PressAnnouncements/ucm410585.htm -
Evidence Mounting for Eliglustat in Gaucher's Disease
SAN DIEGO — Eliglustat (Cerdelga, Genzyme), a new oral treatment for type 1 Gaucher's disease, works almost as well as intravenous enzyme replacement therapy with imiglucerase, new research shows. "It provides a new treatment option for our patients,"
Source: http://www.medscape.com/viewarticle/834451
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http://en.wikipedia.org/wiki/Gaucher%27s_disease
http://www.nlm.nih.gov/medlineplus/gauchersdisease.html
http://www.mayoclinic.org/diseases-conditions/gauchers-disease/basics/definition/CON-20031396
http://www.gaucherdisease.org/
http://www.ninds.nih.gov/disorders/gauchers/gauchers.htm