Family fights to save child with rare genetic disorder FOP
Ali McKean was born with a very rare genetic disorder called Fibrodysplasia Ossificans Progressiva (FOP). It took a large team of doctors more than 5 years t.
Latest news about fop bone disease
US FDA grants orphan drug status to La Jolla Pharma's LJPC-6417
LJPC-6417 is a kinase inhibitor targeting the bone morphogenetic protein (BMP) type-1 receptor, which is mutated in FOP. FOP is a progressive and debilitating genetic disorder characterized by heterotopic ossification. The defining sign present at